Challenges and Opportunities in Rare Pediatric Drug Development

From World Orphan Drug Congress 2021

Date: April 28, 2021

Presenters:
Barry Mangum, PharmD, FCP, Paidion
Betsy Reid, Paidion
Kristi Norris, PhD, Camargo

---

Over half of all rare diseases impact children. In this webinar, we’ll explore the pediatric drug development landscape and answer several key questions:

• Why is pediatric research important, and how is the life sciences industry evolving to address the research gap?
• What regulatory considerations are critical to success for development and approval of a new treatment for a rare pediatric disease?
• What can be done to improve pediatric clinical trials for children with rare diseases?